Myotonic dystrophy type 1 (DM1) is the most common form of adult-onset muscular dystrophy, affecting about 1 in 8,000 people.

Myotonic dystrophy type 1 (DM1) is the most common form of adult-onset muscular dystrophy, affecting about 1 in 8,000 people.

CAMBRIDGE, Mass.--(BUSINESS WIRE)--Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today shared progress in the Phase 1/2 multiple ascending dose ...

Muscular dystrophy is a group of conditions that damage and weaken your muscles over time. Symptoms, age of onset, and outlook depend on the type of muscular dystrophy you have. Muscular dystrophy ...

The most common prodromal symptom of Parkinson disease among community-dwelling older adults was cognitive deficit, followed by subthreshold parkinsonism, urinary dysfunction, and olfactory ...

Nippon Shinyaku Co. Ltd. has disclosed compounds inhibiting binding between r (CUG) repeats in DMPK (DM1) and MBNL protein reported to be useful for the treatment of myotonic dystrophy 1.

TORONTO--(BUSINESS WIRE)-- Satellos Bioscience Inc. (MSCL:CA) (TSX: MSCL, OTCQB: MSCLF) (“Satellos” or the “Company”), a clinical-stage biotechnology company developing life-improving medicines to ...

First returning adult patient from Phase 1b study recently dosed; additional returning patients being scheduled 11-month open-label study will evaluate functional outcomes, safety, muscle composition ...

Grip strength increased 118.6% and predicted forced vital capacity increased 5.8%; whereas, both decline in natural history “Satellos’ new and updated clinical results from the 28-day clinical study ...

Adults with Duchenne muscular dystrophy demonstrated functional improvements exceeding natural history, following 28-day treatment with SAT-3247 Grip strength increased 118.6% and predicted forced ...