12hon MSN
This 11-year-old has battled a rare disease for years — a breakthrough drug helped deliver relief
Actor turned rare disease advocate Luke Rosen tells how his daughter, Susannah, lives with a KIF1A-associated neurological ...
Jonathan Hughes, diagnosed with rare Progressive Supranuclear Palsy, pursues his dream of completing a 5K race with community ...
A new study reveals a critical vulnerability in a brain receptor targeted by a rare autoimmune disease. Researchers have ...
Jan 28 (Reuters) - Regenxbio said on Wednesday the U.S. Food and Drug Administration has placed a clinical hold on two of its ...
No standard treatments for the sometimes deadly disorder have been developed, but that may change due to the newly published research.
2026 is shaping up to be a pivotal year for rare disease drugmakers, with key approvals, filings and readouts lined up for ...
Virginia Tech researchers discovered an indication hidden in the brain that may help doctors identify children suffering from ...
Two people have died and a third remains under investigation after health officials in Hood River County identified multiple cases of Creutzfeldt-Jakob disease (CJD), a rare but deadly brain disorder ...
A "gene silencer" (technically known as small interfering RNA, or siRNA), locally delivered by nanoparticles embedded in an ...
4don MSN
In rare cases, autoantibodies can cause severe reactions to a discontinued Chikungunya vaccine
A new study published in the Proceedings of the National Academy of Sciences suggests that rare cases of brain inflammation ...
For some time, we've known that it's rare to see people with both cancer and Alzheimer's disease. Now, scientists believe ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results